11/14/2025
The Time is NOW! Join the Fight to Bring Hope to HD Families: Urge the FDA to Uphold Accelerated Approval!
Huntington's Disease Society of America, Help 4 HD International, HD Reach, Huntington's Disease Foundation and HDYO have joined forces on a petition directly to the FDA.
Key Asks of the FDA:
Honor Your Previous Guidance: Fully uphold the previously agreed-upon accelerated approval pathway for AMT-130, including the use of external control data from natural history studies.
Recognize the Urgency: Acknowledge the dire, unmet medical need in the HD community and act with the expediency that Breakthrough Therapy and RMAT designations demand.
Expedite Review: Make the review and approval of AMT-130, and any other future HD therapies, a top priority to get this potentially life-altering therapy to patients without further delay.
Sign the Petition Today! Don’t forget to confirm your email to make it count.
https://www.change.org/p/bring-hope-to-huntington-s-disease-families-urge-the-fda-to-uphold-accelerated-approval?source_location=search